Health and Parenting
Patients in the hospital receive gifts under the lights of a Christmas tree

Not home for the holidays? How you can help inpatient families

There’s nothing like being home for the holidays. But for families with a child in the hospital, being home might be a distant dream. As a friend or family member, you may wonder what you can do to make the holidays a little brighter. For ideas, we turned to those who have been there before ... Read More about Not home for the holidays? How you can help inpatient families
Health and Parenting
bottles of opioids

Opioids for acute pain in kids: Four things to know

According to the Centers for Disease Control and Prevention, an estimated 130 Americans die every day from an opioid overdose. Opioid use disorder can include addiction to heroin, as well as to fentanyl and other prescription opioid analgesics. In fact, research suggests that nearly 80 percent of heroin users report using prescription opioids first. It’s ... Read More about Opioids for acute pain in kids: Four things to know
Patient Stories
Noah, who had a biventricular repair, sits on the back of an RV with his brother

Noah the brave: A cross-country quest for a biventricular repair

If you walked down Binney Street next to Boston Children’s hospital this fall, you might’ve noticed something a bit out of the ordinary. Parked on the sidewalk, just out of the way of passers-by, sat a large RV. On the back of the camper, a large photo of a smiling 5-year-old Noah Alderson told part ... Read More about Noah the brave: A cross-country quest for a biventricular repair
Our Community
Woman addresses patients at Transplant Family Dayand families at celebration.

The Transplant Center’s Family Celebration Day 2019 is filled with inspiration

High school prom. College graduation. Wedding. Honeymoon. Job. These are just some of the plot points from Erin Geraghty’s life. While to her they just feel like ‘normal’ accomplishments, to other transplant families her ability to live such a “typical” life gives them hope for their own happy ending.  Erin received a heart transplant at Boston ... Read More about The Transplant Center’s Family Celebration Day 2019 is filled with inspiration
Research
VTP50469, an experimental agent for MLL-rearranged leukemia

Targeted small-molecule agent shows early promise against a dangerous infant leukemia

Leukemias involving reshuffling or rearrangement of the mixed lineage leukemia (MLL) gene, known as MLL-rearranged or MLL-r leukemias, account for 70 to 80 percent of acute leukemias in infants under one year old. In these blood cancers, a subset of acute myeloid and acute lymphoid leukemias (AML and ALL), the MLL gene breaks and reattaches ... Read More about Targeted small-molecule agent shows early promise against a dangerous infant leukemia
Research
sickle cell disease

Gene therapy to boost fetal hemoglobin continues to do well in sickle cell trial

A pilot gene therapy treatment for sickle cell disease, restoring patients’ ability to make fetal hemoglobin, has produced good results in the first three patients to receive it. Investigators at Boston Children’s Hospital reported the findings of their ongoing clinical trial this week at the American Society of Hematology (ASH) annual meeting. The three adult ... Read More about Gene therapy to boost fetal hemoglobin continues to do well in sickle cell trial