Archive for muscular dystrophy
In a thriving gene therapy program, nursing leadership is the driving force
Gene therapy was made possible by decades of technological advances. But to execute gene therapy at scale? That would not be possible without the foresight, organization, and innovation of nursing leadership at Boston Children’s Hospital. The gene therapy implementation framework they have built has become a gold standard for the field. Founded in 2010, the ... Read More about In a thriving gene therapy program, nursing leadership is the driving force
Lucas receives gene therapy for DMD and finds his super muscles
Lucas Toro has a lot in common with Gekko, the cartoon character from PJ Masks. They’re both “little guys” whose strength surprises people. And they both use their muscles for good. Getting strong is a new feeling for Lucas — one he’s using to blaze new trails for other kids. In September 2023, he became ... Read More about Lucas receives gene therapy for DMD and finds his super muscles
Minimally invasive approaches help ease Sydney’s chronic pain
Sydney Hart wants to reimagine the traditional “handicap” symbol. In her online shop, she offers pins, stickers, and other products that infuse the classic wheelchair silhouette with yin-yang symbols, LGBTQ and transgender flags, and even sassy devil horns. “I hope that having symbols with more character will open up the conversation and humanize people with ... Read More about Minimally invasive approaches help ease Sydney’s chronic pain
The neurology resident that could
Elizabeth Engle used to wait in peoples’ driveways until midnight, hoping to enroll them in her genetic studies of eye-movement disorders. She landed there by chance: during her neurology residency, she saw a little boy whose eyes were frozen in a downward gaze. Wanting to find a solution to a disorder that others had written ... Read More about The neurology resident that could