Search Results for: dana-farber boston children's
It’s personal: How the Boston Children’s progeria research community brought new life to an old drug
In late November, the U.S. Food and Drug Administration (FDA) approved a repurposed cancer drug called lonafarnib to treat Hutchinson-Gilford …Read More
Nurses Week 2021: Nurse-led contact tracing team helps reduce the spread of COVID-19
As COVID-19 evolved into a serious threat in March 2020, protecting the health of patients, families, and employees at Boston …Read More
Mapping ‘neighborhoods’ in aggressive childhood brain tumors
The third-most common kind of childhood brain tumor, supratentorial ependymoma, is an aggressive cancer that often returns after surgery and …Read More
A true hero’s journey: How a team approach helped Wolfie overcome pancreatitis
Wolfgang, affectionately known as “Wolfie,” is a bright and energetic 7-year-old with a quick wit and a love for making …Read More
Tough cookie: Steroid therapy helps Alessandra thrive with Diamond-Blackfan anemia
Two-year-old Alessandra is many things. She’s sweet, happy, curious, and, according to her parents, Ralph and Irma, a budding food …Read More
A new druggable cancer target: RNA-binding proteins on the cell surface
In 2021, research led by Ryan Flynn, MD, PhD, and his mentor, Nobel laureate Carolyn Bertozzi, PhD, opened a new …Read More
A small act of kindness: Blood donations get Sadie off the sidelines after her aplastic anemia diagnosis
In March of 2024, Sadie’s life was interrupted. A busy high school senior with classes to attend, soccer matches to …Read More
Could a pill treat sickle cell disease?
The new gene therapies for sickle cell disease — including the gene-editing treatment Casgevy, based on research at Boston Children’s …Read More
Cerebral adrenoleukodystrophy: How the Cooksons dodged a devastating disease
Heather Cookson believes that if she hadn’t insisted her son Ricky get a brain MRI to investigate his frequent headaches, …Read More
Gene therapy for adrenoleukodystrophy: Studies find both risks and benefits
Cerebral adrenoleukodystrophy (CALD), portrayed in the film Lorenzo’s Oil, is a devastating disorder caused by a mutation on the X …Read More